The clinical trial for MPS II gene therapy is expected to start by the end of 2017. Since Nationwide Children’s Hospital is a public service, it relies heavily on patient parent funding. The MPS II community needs to raise $2.5 Million to manufacture the vector and fund the Phase I trial.
Project Alive is a 501(c)(3) non-profit organization dedicated to cure Hunter Syndrome / Mucopolysaccharidosis II through research and advocacy. It is parent funded and 100% contributions go towards MPS II gene therapy research. (IRS Tax ID# 46-4617970). Donate in honor of Noah Nguyen at www.gofundme.com/projectalive
Together was can make this happen. Thank you. God bless.